Total number of publications: 44
2026
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Oral deucrictibant for on-demand treatment of hereditary angioedema attacks (RAPIDe-1): a randomised, double-blind, placebo-controlled, phase 2 trial
MAURER Marcus STOBIECKI Marcin VALERIEVA Anna HAKL Roman STAEVSKA Maria T BOUILLET Laurence DU-THANH Aurélie KESSEL Aharon KIANI-ALIKHAN Sorena MAGERL Markus RESHEF Avner BAEZA Maria Luisa FAIN Olivier FARKAS Henriette GREVE Jens GUILARTE Mar JACOBS Joshua S LI H Henry LLEONART Ramon MANNING Michael E SUSSMAN Gordon L ANDERSON John CHAPDELAINE Hugo COHN Danny M HAGIN David KRÁLÍČKOVÁ Pavlína RITCHIE Bruce SPADARO Giuseppe STAUBACH Petra TARZI Michael D YANG William H MARIE-HELENE Jouvin CRABBÉ Rafael LEEUWEN Simone van CHEN Huaihou ZHU Li KNOLLE Jochen LESAGE Anne LU Peng RIEDL Marc A AYGÖREN-PÜRSÜN Emel
Peer-reviewed scientific article
Lancet Haematolgy, year: 2026, volume: 13, edition: 4, DOI
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Oral deucrictibant for on-demand treatment of hereditary angioedema attacks (RAPIDe-1): a randomised, doubleblind,-controlled, 2 trial
MAURER Marcus STOBIECKI Marcin VALERIEVA Anna HAKL Roman STAEVSKA Maria T BOUILLET Laurence DU-THANH Aurélie KESSEL Aharon KIANI-ALIKHAN Sorena MAGERL Markus RESHEF Avner BAEZA Maria Luisa FAIN Olivier FARKAS Henriette GREVE Jens GUILARTE Mar JACOBS Joshua S LI H Henry LLEONART Ramon MANNING Michael E SUSSMAN Gordon L ANDERSON John CHAPDELAINE Hugo COHN Danny M HAGIN David KRÁLÍČKOVÁ Pavlína RITCHIE Bruce SPADARO Giuseppe STAUBACH Petra MICHAEL D Tarzi YANG William H JOUVIN Marie-Helene CRABBÉ Rafael SIMONE van Leeuwen CHEN Huaihou ZHU Li KNOLLE Jochen LESAGE Anne LU Peng RIEDL Marc A AYGÖREN-PÜRSÜN Emel
Peer-reviewed scientific article
LANCET HAEMATOLOGY, year: 2026, volume: 13, edition: 4, DOI
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Registry-Based Analysis of Treatment and Retreatment Attacks of Hereditary Angioedema
HAKL Roman BAROŠ Jan SOBOTKOVÁ Marta ZACHOVÁ Radana KRÁLÍČKOVÁ Pavlína VACHOVÁ Martina KRČMOVÁ Irena SVOBODA Michal SZMUCOVÁ Vendula SKOTÁKOVÁ Monika LITZMAN Jiří
Peer-reviewed scientific article
Clinical & Experimental Allergy, year: 2026, DOI
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Sebetralstat for on-demand treatment of hereditary angioedema: A pooled analysis of placebo-controlled clinical trials
AYGÖREN-PÜRSÜN Emel COHN Danny M AGMON-LEVIN Nancy BANERJI Aleena BERNSTEIN Jonathan A BUSSE Paula CANCIAN Mauro CASTRO Eunice Dias de FARKAS Henriette GRIVCHEVA-PANOVSKA Vesna HAGIN David HAKL Roman HONDA Daisuke KESSEL Aharon KINACIYAN Tamar IFAAD KUROWSKI Marcin LI H Henry LLEONART Ramon LONGHURST Hilary J LUMRY William R MAGERL Markus MARTINEZ-SAGUER Inmaculada MELAMED Isaac PSARROS Fotis SAVIC Sinisa SOTERES Daniel F STAEVSKA Maria STOBIECKI Marcin WEDNER H James ZANICHELLI Andrea HAO James PATIL Ketan IVERSON Matthew OWIREDU-YEBOA Samuel SMITH Michael D YEA Christopher M AUDHYA Paul K RIEDL Marc A KIANI-ALIKHAN Sorena MAURER Marcus
Peer-reviewed scientific article
World Allergy Organization Journal, year: 2026, volume: 19, edition: 7, DOI
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The 2025 WAO Guidelines for the classification, diagnosis, and treatment of hereditary angioedema, with consideration of worldwide disparities
VÁZQUEZ Daniel O GIAVINA-BIANCHI Pedro JOSVIACK Darío KAPLAN Allen P AS Pablo MARTINEZ FANTINI Claudio BERNSTEIN Jonathan A ABBAS Shahid LEVIN Nancy Agmon AL-AHMAD Mona ALANDIJANI Sultan ALHASHMI Hani Abdullah ALI Ramzy Mohammed ALLAM Ines AL-MANSOURI Maryam Al-Nesf AL-TAMEMI Salem ALTRICHTER Sabine CASTELLÓ Mirta Álvarez ANDOH Hilary D AUN Marcelo Vivolo MAPONDELA Kassim Babu BANERJI Aleena NOÉMI-ANNA Bara BARRERA Olga Melcina PERIGAULT Paulo Barrera BRANCO-FERREIRA Manuel CALDERÓN-LLOSA Oscar Manuel CANONICA Giorgio Walter ALMARALES Raúl Castro CECCHI Lorenzo YOON-SEOK Chang CHANTAPHAKUL Hiroshi CHIKOVANI Tinatin CHONG-NETO Herberto Jose CONTRERAS-VERDUZCO Francisco Alberto DEFENDI Federica DORSAINVIL Vilbrun EBISAWA Motohiro EL-SAYED Zeinab A FASANO Mary Beth FAZLOLLAHI Mohammad Reza FEMINE Euguens FERNANDES Fátima Rodrigues FIOCCHI Alessandro FONACIER Luz GALLEGO Claudia ABUJETA José Luis García GEREDA José Enrique GIORDANO Erminia GÖKMEN Nihal Mete GÓMEZ R Maximiliano GONZALEZ Monica DÍAZ Sandra González GRAU Masumi HAKL Roman HIDE Michihiro HOSSNY Elham HUILAJA Laura HUQ Syed Rezaul IRANI Carla ISHCHANKA Aksana ISPAYEVA Zhanat JAMALYAN Kristina R KAIDASHEV Igor KAMKAMIDZE George TANNO Luciana Kase KATHURIA KESSEL Aharon KIANI-ALIKHAN Sorena KOMARLA Nagendra Prasad KVEDARIENE Violeta LANG David M LEE Yonh Won LEVIN Michael LI Philip H LI Henry LUMRY William R MACHAVARIANI Ketevan MARTINEZ-SAGER Inmaculada MASELLI Juan P MIKOS Nikolaos MITSKEVICH Nunu MS Hassan MOBAYED ORTEGA Olga Patricia Monge MORITA Hideaki MUNKHBAYARLAKH Sonomjamts NABAVI Mohammad NAQVI Muhammad Raza OCAMPO Jaime OLIVARES Margarita ORTEGA-MARTELL Jose Antonio OYUNTSATSRAL Batsaikhan PAPADOPOULOS Nikos PATELLA Vincenzo PAWANKAR Ruby PETER Jonny PSARROS Fotis REGATEIRO Frederico REIDL Marc RIGALT Ann M FERNÁNDEZ Jenny Mariel Rincón GÓMEZ Maria Antonia Rivera GUTIÉRREZ María Isabel Rojo SAHINER Ümit Murat SANDOVAL-RUBALLOS Mónica SANTOS Natacha SARRAZOLA Mauricio SCHRIJVERS Rik SHCHUROK Iryna SHEIKH Farrukh Rafique SOBOTKOVA Marta SORIA Angele STEFANAKI Efthalia TARAZONA Robin LUJÁN Alejandra Valecillos ROSTAN Marylin Valentin VALERIEVA Anna WONG Gary Wing-Kin FK Patrick YONG ZAITOUN Fares MARTIN Bryan L ANSOTEGUI Ignacio J MORAIS-ALMEIDA Mário CRAIG Timothy J
Peer-reviewed scientific article
World Allergy Organization Journal, year: 2026, DOI
2025
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Angioedém jako nežádoucí účinek léčby různými farmaky
BAROŠ Jan HAKL Roman PEŠÁK Sáva CHOVANCOVÁ Zita
Peer-reviewed scientific article
Vnitřní lékařství, year: 2025, volume: 71, edition: 8, DOI
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Becoming attack-free further improves health-related quality of life in patients with hereditary angioedema receiving garadacimab
STAUBACH Petra CRAIG Timothy J FUKUDA Tomoo AYGOREN-PURSUN Emel HAKL Roman BRAVERMAN Julia LAWO John-Philip POLLEN Maressa NENCI Chiara LI Philip H FARKAS Henriette
Peer-reviewed scientific article
ALLERGY AND ASTHMA PROCEEDINGS, year: 2025, volume: 46, edition: 3, DOI
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Case report: challenges in a long-term prophylaxis in hereditary angioedema (HAE)
BAROŠ Jan HAKL Roman LITZMAN Jiří
Conference abstract
Year: 2025, type: Conference abstract
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First report from the Czech national registry of inborn errors of immunity (2012-2025)
CHOVANCOVÁ Zita HLAVÁČKOVÁ Eva HAKL Roman MILOTA Tomas KRALICKOVA Pavlina MALKUSOVA Ivana HUTYROVA Beata SAFAROVA Michaela VYDLAKOVA Jana JILEK Dalibor NOVAK Jiri SCHNEIDEROVÁ Helena KRALOVA Petra ZIMULOVA Alena NOVAK Vitezslav BYSTRON Jaromir ZAVESKA Dita LATALOVA Vendula KOPRIVA Frantisek KASL Milan KRACIK Vladimir FORMANKOVA Renata SEDLACEK Petr VYTISKOVA Karolina SVOBODA Michal NOVAKOVA Hana LITZMAN Jiří
Peer-reviewed scientific article
Frontiers in immunology, year: 2025, volume: 16, edition: September 2025, DOI
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Unmet needs in hereditary angioedema: an international survey of physicians
BUTTGEREIT Thomas AULENBACHER Felix ADATIA Adil AYALA Carolina Vera AL-NESF Maryam Ali ALTRICHTER Sabine ABUZAKOUK Mohamed AL-AHMAD Mona ALI Ramzy Mohammed BERARDI Alejandro BOCCON-GIBOD Isabelle BOUILLET Laurence BRUSSINO Luisa BARESIC Marko BUSSE Paula J BETSCHEL Stephen D CHONG-NETO Herberto LLOSA Oscar Calderon CRAIG Timothy J DORR Anthony D JUNIOR Sergio Duarte Dortas FOMINA Daria FARKAS Henriette FOK Jie Shen GRUMACH Anete S GREVE Jens GUILARTE Mar GONCALO Margarida GRIVCHEVA-PANOVSKA Vesna HIDE Michihiro HAKL Roman JINDAL Ankur KATELARIS Constance H KAMALESWARAN Shailajah KINACIYAN Tamar LATYSHEVA Elena SOUSA Jose Ignacio Larco BELLFILL Ramon Lleonart MOBAYED Hassan METZ Martin NASR Iman MITREVSKA Natasa T NICOLA Stefania PARISI Claudio Alberto Salvador POREBSKI Grzegorz PETER Jonny FERRIANI Mariana Paes Leme FILHO Nelson Rosario SEKEREL Buelent Enis SERPA Faradiba Sarquis STOBIECKI Marcin TRAINOTTI Susanne VALERIEVA Anna WONGSA Chamard WONG Jane C Y YUCEL Esra LI Yinglei NENCI Chiara MAURER Marcus MAGERL Markus LI Philip H
Peer-reviewed scientific article
Orphanet Journal of Rare Diseases, year: 2025, volume: 20, edition: 1, DOI